5 Biggest Biotechnology Companies in the World

3. Vertex Pharmaceuticals Incorporated (NASDAQ:VRTX)

Market Cap: $105.31 billion

Vertex Pharmaceuticals Incorporated (NASDAQ:VRTX), founded in 1989 in Boston, MA, is known for cystic fibrosis drugs like Kalydeco, Orkambi, Symdeko, and Trikafta/Kaftrio. They also target infectious diseases, autoimmune diseases, cancer, and neurological disorders. Diversification includes Casgevy for beta-thalassemia and sickle-cell disease. In Q4 2023, Vertex Pharmaceuticals Incorporated (NASDAQ:VRTX)’s revenue exceeded guidance by $7.9 million, reaching $154.9 million.